re: Treatment for infant muscle wasting disease to hit market. potential price: $2 million

I am sure people realize that this treatment is not a pill but actual gene therapy.

Here's a link on that means:

LINK /

Here's also a link on Zolgensma.

LINK /

BTW, Novartis bought AveXis, which I believe was the primary R&D arm for Zolgensma prior to purchase for 8.7bn.

The market will dictate the costs and for now this is the cost of business to take on rare diseases in our society.

You could always go to another country or market where there is no research done but you can get advil for free.